{"id":9220,"date":"2022-12-20T23:57:32","date_gmt":"2022-12-20T23:57:32","guid":{"rendered":"https:\/\/www.ptcbio.com\/?page_id=9220"},"modified":"2026-03-25T13:07:30","modified_gmt":"2026-03-25T17:07:30","slug":"our-science","status":"publish","type":"page","link":"https:\/\/www.ptcbio.com\/our-science\/","title":{"rendered":"Our Science"},"content":{"rendered":"
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\n\t\t\t\t\t\t\t\t\t\t\t\tOur Science<\/span>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\tPioneering Innovation<\/span>\n\t\t\t\t\t\t\t\t\t\t\t<\/h1>\n\t\t\t\t\t\t\t\t\t\t\t\t\t
Our research is centered on two scientific platforms\u2014Splicing and Inflammation and Ferroptosis<\/div>\n\t\t\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t<\/div>\n\n\t
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  1. \n\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\tHomepage<\/span>\n\t\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t<\/li>\n\t\t\t\t\t\t\t\t\t\t\t\t
  2. \n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\tOur Science<\/span>\n\t\t\t\t\t\t\t<\/span>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t<\/li>\n\t\t\t\t\t\t<\/ol>\n<\/nav>\n<\/div>\n\n\n\n
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    We have focused our research efforts on two scientific platforms\u2014splicing and inflammation and ferroptosis \u2014 where PTC has unique expertise to discover and advance to the clinic innovative therapies.\u200b<\/p>\n\n\n

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    Our Scientific Platforms<\/h2>\n\t\t\t<\/span>\n\t\t<\/div>\n\t\n\t
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    \n\t\t\t\t\t\tSplicing<\/span>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t
    \n\t\t\t\t\t\tModulating splicing to control protein production\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\tLearn more<\/a>\n\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t\t\t\t\n\t\t\t
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    \n\t\t\t\t\t\tInflammation & Ferroptosis<\/span>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t
    \n\t\t\t\t\t\tTargeting oxidative stress and inflammation pathways\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\tLearn more<\/a>\n\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t\t<\/div>\n<\/div>\n\n\n
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    \n\t\t\t\tOur Products\t\t\t<\/div>\n\t\t\n\t\t\t\t\t

    \n\t\t\t\tLeveraging our unique scientific knowledge<\/span>\n\t\t\t<\/h2>\n\t\t\n\t\t
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    We have a <\/span>number of<\/span>\u00a0potentially promising therapies for rare\u00a0<\/span><\/span>neurologic and metabolic conditions.<\/span><\/span>\u200b<\/span><\/p>\n\t\t<\/div>\n\n\t\t\n\t\t\t

    \n\n\t\t\t\t\tExplore our Products<\/a>\n\t\t\n\t\t\n\t\t\n\t<\/div>\n\n\t<\/div>\n<\/div>\n\n\n\n\n
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    Read More About Science and Innovation at PTC<\/h3>\n\t\t
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    \n\t\t\t\t\"Ferroptosis\t\t\t<\/div>\n\n\t\t\t\n\t\t\t
    \n\t\t\t\tWhat You Need to Know About Ferroptosis & Friedreich’s Ataxia (FA)\t\t\t<\/div>\n\n\t\t\t
    \n\t\t\t\tAn Informative Q&A with Jonathan Cherry, Global Project Leader Our research efforts at PTC are focused on two scientific platforms…\t\t\t<\/div>\n\t\t<\/div>\n\n\t\tRead More<\/span>\n\t<\/a>\n<\/div>\n\n
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    \n\t\t\t\t\"Ferroptosis\t\t\t<\/div>\n\n\t\t\t\n\t\t\t
    \n\t\t\t\tWhat You Need to Know About Ferroptosis\t\t\t<\/div>\n\n\t\t\t
    \n\t\t\t\tOur research efforts at PTC are focused on two scientific platforms \u2013 splicing and inflammation and ferroptosis \u2013 where PTC has unique…\t\t\t<\/div>\n\t\t<\/div>\n\n\t\tRead More<\/span>\n\t<\/a>\n<\/div>\n\n
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    \n\t\t\t\t\"PTC's\t\t\t<\/div>\n\n\t\t\t\n\t\t\t
    \n\t\t\t\tA Whole Team in One Molecule: PTC\u2019s Splicing Platform\t\t\t<\/div>\n\n\t\t\t
    \n\t\t\t\tThere are many things that make PTC Therapeutics truly unique, and the splicing platform is one of them. Here, \u201csplicing\u201d refers to…\t\t\t<\/div>\n\t\t<\/div>\n\n\t\tRead More<\/span>\n\t<\/a>\n<\/div>\n\n
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    \n\t\t\t\t\"Calum\t\t\t<\/div>\n\n\t\t\t\n\t\t\t
    \n\t\t\t\tAn Important Job and Rewarding Career\t\t\t<\/div>\n\n\t\t\t
    \n\t\t\t\tIt\u2019s Calum Sinclair\u2019s job to help ensure patient safety. As the Vice President, Global Pharmacovigilance (PV) at PTC, Calum leads a…\t\t\t<\/div>\n\t\t<\/div>\n\n\t\tRead More<\/span>\n\t<\/a>\n<\/div>\n\n\t<\/div>\n<\/div>\n\n","protected":false},"excerpt":{"rendered":"

    We have focused our research efforts on two scientific platforms\u2014splicing and inflammation and ferroptosis \u2014 where PTC has unique expertise to discover and advance to the clinic innovative therapies.\u200b<\/p>\n","protected":false},"author":2,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"class_list":["post-9220","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"\nPTC Therapeutics' Scientific Platforms<\/title>\n<meta name=\"description\" content=\"Discover PTC Therapeutics' platforms, and our unique expertise to discover and advance innovative therapies for rare diseases with high unmet need.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.ptcbio.com\/our-science\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Our Science\" \/>\n<meta property=\"og:description\" content=\"Discover PTC Therapeutics' platforms, and our unique expertise to discover and advance innovative therapies for rare diseases with high unmet need.\" \/>\n<meta property=\"og:url\" content=\"https:\/\/www.ptcbio.com\/our-science\/\" \/>\n<meta property=\"og:site_name\" content=\"PTC Therapeutics (United States)\" \/>\n<meta property=\"article:publisher\" content=\"https:\/\/www.facebook.com\/PTCTherapeutics\" \/>\n<meta property=\"article:modified_time\" content=\"2026-03-25T17:07:30+00:00\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:site\" content=\"@PTCBio\" \/>\n<meta name=\"twitter:label1\" content=\"Est. reading time\" \/>\n\t<meta name=\"twitter:data1\" content=\"1 minute\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\\\/\\\/schema.org\",\"@graph\":[{\"@type\":\"WebPage\",\"@id\":\"https:\\\/\\\/www.ptcbio.com\\\/our-science\\\/\",\"url\":\"https:\\\/\\\/www.ptcbio.com\\\/our-science\\\/\",\"name\":\"PTC Therapeutics' Scientific Platforms\",\"isPartOf\":{\"@id\":\"https:\\\/\\\/www.ptcbio.com\\\/#website\"},\"datePublished\":\"2022-12-20T23:57:32+00:00\",\"dateModified\":\"2026-03-25T17:07:30+00:00\",\"description\":\"Discover PTC Therapeutics' platforms, and our unique expertise to discover and advance innovative therapies for rare diseases with high unmet need.\",\"breadcrumb\":{\"@id\":\"https:\\\/\\\/www.ptcbio.com\\\/our-science\\\/#breadcrumb\"},\"inLanguage\":\"en-US\",\"potentialAction\":[{\"@type\":\"ReadAction\",\"target\":[\"https:\\\/\\\/www.ptcbio.com\\\/our-science\\\/\"]}]},{\"@type\":\"BreadcrumbList\",\"@id\":\"https:\\\/\\\/www.ptcbio.com\\\/our-science\\\/#breadcrumb\",\"itemListElement\":[{\"@type\":\"ListItem\",\"position\":1,\"name\":\"Home\",\"item\":\"https:\\\/\\\/www.ptcbio.com\\\/\"},{\"@type\":\"ListItem\",\"position\":2,\"name\":\"Our Science\"}]},{\"@type\":\"WebSite\",\"@id\":\"https:\\\/\\\/www.ptcbio.com\\\/#website\",\"url\":\"https:\\\/\\\/www.ptcbio.com\\\/\",\"name\":\"PTC Therapeutics, Inc.\",\"description\":\"Translating Science. 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